Verified
Health
Emma tells her story
Calm, sincere tone

I have a rare disease. There's treatment out there. There's hope for a cure. But I can't afford it.

EM

Emma's Family

Austin, Texas • Organized by Emma's parents

$200,000
goal: $10,000,000
1,247 supporters 45 days left

Watch the video and see why this help is my only shot.

Emma tells her story (1min30s - 2min) | Calm, sincere tone

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What Spinal Muscular Atrophy (SMA) Really Is

SMA is a rare and serious genetic disease that affects the motor neurons - basically the parts that control how your body moves. As time goes on, it causes:

  • Your muscles to get progressively weaker
  • Trouble walking, swallowing, and breathing
  • You lose your independence
  • It's actually life-threatening if you don't get treatment

Without the right treatment, the disease just keeps getting worse.

The Treatment and Real Hope

Today, there's this cutting-edge, super-specific treatment that's been developed to target the exact genetic cause of SMA.

Here's what this treatment does:

  • It tackles the genetic problem that's causing the disease
  • Stops the disease from progressing
  • Helps you gradually get your function back
  • Gives you a real shot at stabilizing and getting significantly better

Where Your Money Goes

Every single donation goes straight to:

  • Getting the expensive medication
  • Hospital stays and specialist care
  • Genetic testing and check-ups
  • The whole medical team
  • All the care needed during treatment